CS Blogs

QUINCY, Mass., Sept. 30, 2024 /PRNewswire/ -- Today, the National Organization for Rare Disorders (NORD®) announced two new requests for proposal (RFP) for…

Alnylam Pharmaceuticals, Inc. News− Echocardiographic and Cardiac Biomarker Data From the HELIOS-B Study Presented Today Support the Potential of Vutrisiran in…

People with hereditary transthyretin amyloidosis (hATTR), a group of diseases that includes familial amyloid polyneuropathy (FAP), have significantly shorter nerve…

The National Organization for Rare Disorders (NORD) announced two new requests for proposal (RFP) for grant funding related to Amyloidosis and Levy-Yeboa Syndrome (…

In collaboration with F Hoffmann-la Roche & Co Ltd we have developed a new chemical entity, carboxy pyrrolidone hexanoyl pyrrolidone carboxylic acid (CPHPC),…

Key takeaways:ALXN2220, a novel investigational depleter monoclonal antibody, was granted fast track designation by the FDA.It is designed for the treatment of…

BackgroundImmunoglobulin light-chain amyloidosis is a relatively rare condition with a worldwide incidence of 5.1–12.8 cases per million person-years (Baker, 2022…

A 71-year-old healthy White male presented in 2010 with intermittent redness in the right eye nasally for 10 years. On examination, corrected visual acuity was 20/…

The FDA has granted 510(k) clearance to a Centiloid scaling apparatus software for positron emission tomography-based amyloid imaging to evaluate individuals for…

Amyloidosis is a localized or systemic disease caused by deposition of proteins in the extracellular space of various organs and tissues. As part of the disease,…