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EMPOWER CHANGEYour Voice Matters in Building a Rare Disease Advisory CouncilJoin the coalition of rare disease patients, experts, and advocates like you to push…

DelveInsight’s “AL Amyloidosis Market Insights, Epidemiology, and Market Forecast-2034″ report offers an in-depth understanding of the AL Amyloidosis, historical…

Data presented at the 2024 American Heart Association (AHA) Scientific Sessions highlighted that early initiation and continuous use of acoramidis (Attruby;…

“We hope you will join us for SLC6A1 Connect’s 2024 International Scientific Symposium and Family Conference to be held on December 5-6, 2024 at the Omni Hotel in…

Join the LGS Community on December 5th before AES for a special showing of It’s All Your Fault, Tyler Price! – a new musical from Emmy winner Ben Decter (Lucifer)…

The purpose of this symposium is to bring established investigators, junior researchers and industrials together to discuss and expand this exciting area of…

For people living with rare diseases, finding financial help for out-of-pocket cost is vital—the PAN Foundation can help. Join to learn how you can apply for a PAN…

PITTSBURGH, Nov. 26, 2024 /PRNewswire/ -- PANTHERx® Rare, a leader in rare disease product patient access and support services in the United States, is pleased…

On a Zoom call last month from California, BridgeBio CEO Neil Kumar needled a colleague about the remote possibility of the New York Yankees rallying to win the…